Rocket Pharmaceuticals, Inc.
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Rocket Pharmaceuticals, Inc. is a clinical-stage biotechnology company developing gene therapies for rare and devastating diseases. The company focuses on lentiviral vector-based gene therapies and gene editing approaches to treat genetic disorders including Fanconi Anemia, Danon disease, and Pyruvate Kinase Deficiency. Rocket Pharmaceuticals aims to deliver potentially curative treatments through a single administration that addresses the underlying genetic cause of these conditions.